Adam Eliav

Intermittent lipid nanoparticle mRNA administration prevents cortical dysmyelination associated with arginase deficiency

Molecular Therapy — Nucleic Acids · 2022 · 21 citations

Gene therapy for guanidinoacetate methyltransferase deficiency restores cerebral and myocardial creatine while resolving behavioral abnormalities

Molecular Therapy — Methods & Clinical Development · 2022 · 10 citations