
Aravindhan Veerapandiyan
Associate Professor of Pediatrics · University of Arkansas for Medical Sciences (UAMS) College of Medicine
Credentials: · ·
History
- 2018–2019

- 2014–2017
- 2013–2014
2012–2013
Research
AAV gene therapy for Duchenne muscular dystrophy: the EMBARK phase 3 randomized trial
Nature Medicine · 2025 · 143 citations
Subacute Liver Failure Following Gene Replacement Therapy for Spinal Muscular Atrophy Type 1
Case report · The Journal of Pediatrics · 2020 · 110 citations
Journal of Intellectual Disability Research · 2012 · 69 citations

9 papers
- CP
9 papers

9 papers

8 papers

8 papers · 3 as a resident
- SM
8 papers

8 papers

7 papers
Clinical trials
- 2026–2029
Site PI · Recruiting · Phase 1, Phase 2
Precision BioSciences, Inc.
- 2025–2030
Site PI · Recruiting
ITF Therapeutics LLC
- 2025–2030
Trial Readiness and Endpoint Assessment in Pediatric Myotonic Dystrophy Extension
Site PI · Recruiting
Virginia Commonwealth University
- 2024–2031
A Study of SGT-003 Gene Therapy in Duchenne Muscular Dystrophy (INSPIRE DUCHENNE)
Site PI · Recruiting · Phase 1, Phase 2
Solid Biosciences Inc.




