
Chamindra Laverty
Clinical Director of Muscle Disease · University of California (San Diego) Medical Center
Credentials: · · · · ·
History
PresentUniversity of California (San Diego) Medical Center Fellowship
PresentMuscle Disease · University of California (San Diego) Medical Center

2009–2010
2006–2009
Research
Childhood amyotrophic lateral sclerosis caused by excess sphingolipid synthesis
Nature Medicine · 2021 · 135 citations
The Lancet Neurology · 2024 · 113 citations
BAG3 myofibrillar myopathy presenting with cardiomyopathy
Case report · Neuromuscular Disorders · 2015 · First of 10 authors · Corresponding · 70 citations

6 papers

5 papers

4 papers

4 papers · 1 as a fellow

4 papers
- NJ
4 papers

4 papers

4 papers
Clinical trials
- 2024–2031
A Study of SGT-003 Gene Therapy in Duchenne Muscular Dystrophy (INSPIRE DUCHENNE)
Site PI · Recruiting · Phase 1, Phase 2
Solid Biosciences Inc.
- 2019–2026
Estab Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1)
Site PI · Recruiting
Virginia Commonwealth University
- 2018–2038
Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)
Site PI · Recruiting
Novartis Pharmaceuticals



