Eric Crombez

Efficacy of sapropterin dihydrochloride in increasing phenylalanine tolerance in children with phenylketonuria: a phase III, randomized, double-blind, placebo-controlled study

The Journal of Pediatrics · 2009 · 151 citations

The response of patients with phenylketonuria and elevated serum phenylalanine to treatment with oral sapropterin dihydrochloride (6R-tetrahydrobiopterin): a phase II, multicentre,…

Journal of Inherited Metabolic Disease · 2007 · 140 citations