Erika Augustine
Associate Chief Science Officer and Director of the Clinical Trials Unit · Johns Hopkins University School of Medicine
Credentials: · · · · ·
History
- Present
Clinical Trials Unit · Johns Hopkins University School of Medicine
- Present
Kennedy Krieger Institute Center · Johns Hopkins University School of Medicine
- 2003–2007
Neurology
Research
Patient-Customized Oligonucleotide Therapy for a Rare Genetic Disease
Case report · New England Journal of Medicine · 2019 · 642 citations
JAMA · 2015 · 181 citations
Clinical trials in rare disease: challenges and opportunities
Journal of Child Neurology · 2013 · First of 3 authors · 172 citations
45 papers
32 papers
21 papers · 1 as a resident
12 papers
8 papers
8 papers
8 papers
7 papers
Grants
- 2025–2030
Batten Disease Clinical Research Consortium
National Institute of Child Health and Human Development · U54
Contact PI · $3.4M · Hugo w. Moser Res Inst Kennedy Krieger
- 2023–2028
Kennedy Krieger Institute - Johns Hopkins University NeuroNEXT Site
National Institute of Neurological Disorders and Stroke · U24
Contact PI · $1.8M · Hugo w. Moser Res Inst Kennedy Krieger
- 2019–2025
National Institute of Neurological Disorders and Stroke · U01
Contact PI · $3.7M · University of Rochester
- 2011–2016
Phase 2 of CellCept for Treatment of Juvenile Neuronal Ceroid Lipofuscinosis
Food and Drug Administration · R01
Contact PI · $375.5K · University of Rochester
Clinical trials
- 2011–2015
Cellcept for Treatment of Juvenile Neuronal Ceroid Lipofuscinosis
Principal investigator · Completed · Phase 2
University of Rochester