Janet Kwiatkowski
Director of the Thalassemia Center · University of Pennsylvania Health System
Credentials: · ·
History
PresentThalassemia Center · University of Pennsylvania Health System
- 1992–1995
Pediatrics
Research
Gene Therapy in Patients with Transfusion-Dependent β-Thalassemia
New England Journal of Medicine · 2018 · 520 citations
Controlled trial of transfusions for silent cerebral infarcts in sickle cell anemia
New England Journal of Medicine · 2014 · 406 citations
American Society of Hematology 2020 guidelines for sickle cell disease: transfusion support
Blood Advances · 2020 · 385 citations
33 papers
30 papers
28 papers
- PG
21 papers
13 papers
13 papers
- RI
13 papers
10 papers
Grants
- 2022–2023
Eleventh Cooley's Anemia Symposium
National Heart, Lung, and Blood Institute · R13
Contact PI · $10K · New York Academy of Sciences
- 2011–2014
Comparative Effectiveness of Strategies to Improve Iron Chelation in Thalassemia
National Heart, Lung, and Blood Institute · R34
PI · $827.4K · Boston Children's Hospital
- 2000–2011
Thalassemia Clinical Research Network
National Heart, Lung, and Blood Institute · U01
Contact PI · $144.5K · Children's Hosp of Philadelphia
Clinical trials
- 2025–2027
ALS20-101 Lentiviral Gene Therapy for Beta Thalassemia
Principal investigator · Recruiting · Phase 1, Phase 2
Children's Hospital of Philadelphia
- 2015–2019
Principal investigator · Terminated · Phase 4
ApoPharma
- 2014–2019
Efficacy and Safety of Ferriprox® in Patients With Sickle Cell Disease or Other Anemias
Principal investigator · Terminated · Phase 4
ApoPharma
- 2012–2017
Combination Deferasirox and Deferiprone for Severe Iron Overload in Thalassemia
Principal investigator · Completed · Phase 1, Phase 2
Children's Hospital of Philadelphia