Jerry R. Mendell
Advisor to the Jerry R. Mendell Center for Gene Therapy
Credentials: · ·
History
- Present
Research
Single-Dose Gene-Replacement Therapy for Spinal Muscular Atrophy
New England Journal of Medicine · 2017 · First of 26 authors · 1,837 citations
Therapeutic microRNA delivery suppresses tumorigenesis in a murine liver cancer model
Cell · 2009 · 1,437 citations
Evidence-based path to newborn screening for Duchenne muscular dystrophy
Annals of Neurology · 2012 · First of 19 authors · Corresponding · 669 citations
- ZS
84 papers · 12 as a resident
- JK
53 papers
41 papers
40 papers
30 papers
- AP
29 papers
26 papers
25 papers
Grants
- 2011–2018
Vascular Delivery of Alpha-Sarcoglycan for LGMD2D
National Institute of Arthritis and Musculoskeletal and Skin Diseases · U01
Contact PI · $2.1M · Research Inst Nationwide Children's Hosp
- 2012–2018
Training in Neuromuscular Diseases
National Institute of Neurological Disorders and Stroke · T32
PI · $946K · Ohio State University
- 2014–2017
Dual-Vector Mediated Mini-Dystrophin Restoration of Function in Mdx Model of DMD
National Institute of Neurological Disorders and Stroke · R21
Contact PI · $402.9K · Research Inst Nationwide Children's Hosp
- 2010–2017
Overcoming Immune Barriers to Gene Correction for Duchenne Muscular Dystrophy
National Institute of Child Health and Human Development · U54
Contact PI · $6.7M · Research Inst Nationwide Children's Hosp
Clinical trials
- 2018–2023
Limb Girdle Muscular Dystrophy Type 2E Recruitment Study
Principal investigator · Unknown
Nationwide Children's Hospital
- 2016–2019
rAAVrh74.MHCK7.DYSF.DV for Treatment of Dysferlinopathies
Principal investigator · Completed · Phase 1
Sarepta Therapeutics, Inc.
- 2015–2017
Principal investigator · Completed · Phase 1
Jerry R. Mendell
- 2015–2017
Principal investigator · Completed · Phase 1, Phase 2
Jerry R. Mendell