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John Brandsema

Neuromuscular Section Head · University of Pennsylvania Health System

Credentials: · · · · ·

History

University of Pennsylvania Health System
Present
Neuromuscular Fellowship Program Section · Children's Hospital of Philadelphia
Present
University of Pennsylvania Health System
Present

Neuromuscular Medicine
Massachusetts General Hospital
2012–2013
Hospital for Sick Children
2007–2012
DALHOUSIE UNIV, HALIFAX
2003–2007

Research

Cerebral arteriopathy in children with neurofibromatosis type 1
PEDIATRICS · 2009 · 91 citations
Intrathecal Onasemnogene Abeparvovec for Sitting, Nonambulatory Patients with Spinal Muscular Atrophy: Phase I Ascending-Dose Study (STRONG)
Journal of Neuromuscular Diseases · 2023 · 51 citations
Ethical Challenges Confronted When Providing Nusinersen Treatment for Spinal Muscular Atrophy
JAMA Pediatrics · 2018 · 46 citations

Susan Matesanz
8 papers · 1 as a fellow
Craig McDonald
6 papers
Nancy Kuntz
6 papers
Russell Butterfield
6 papers
BD
Basil Darras
5 papers
Craig Zaidman
5 papers
Julie Parsons
5 papers
Kimberly Lin
5 papers
Anne Connolly
4 papers
Carol Wittlieb-Weber
4 papers
Carsten Bonnemann
4 papers
GT
Gihan Tennekoon
4 papers

Clinical trials

A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy
Site PI · Recruiting · Phase 2
argenx
2025–2029
A Study of SGT-003 Gene Therapy in Duchenne Muscular Dystrophy (INSPIRE DUCHENNE)
Site PI · Recruiting · Phase 1, Phase 2
Solid Biosciences Inc.
2024–2031