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Katherine High

Former President, Therapeutics, AskBio · University of Pennsylvania Health System

Credentials: · ·

History

St Jude Children's Research Hospital
Present
University of Pennsylvania Health System
Present

Hematology and Medical Oncology
University of North Carolina at Chapel Hill
1981–1984
Internal Medicine
1978–1981
University of Pennsylvania
University of North Carolina School of Medicine
1974–1978
Harvard University
1968–1972

Research

Successful transduction of liver in hemophilia by AAV-Factor IX and limitations imposed by the host immune response
Nature Medicine · 2006 · 1,778 citations
Safety and efficacy of gene transfer for Leber's congenital amaurosis
New England Journal of Medicine · 2008 · 1,742 citations
Efficacy and safety of voretigene neparvovec (AAV2-hRPE65v2) in patients with RPE65-mediated inherited retinal dystrophy: a randomised, controlled, open-label, phase 3 trial
The Lancet · 2017 · 1,570 citations

Tim Nichols
16 papers
Albert Maguire
11 papers
Nathan Hagstrom
11 papers · 2 as a fellow
AS
Alexander Schlachterman
7 papers · 2 as a resident
Eleanor Pollak
7 papers · 1 as a resident
EP
Eric Pierce
7 papers
Hansell Stedman
7 papers
James Wilson
7 papers
MR
Margaret Ragni
7 papers
BL
Bart Leroy
6 papers
CM
Catherine Manno
6 papers
Alan Flake
5 papers

Grants

Gene Therapy for Hemophilia
National Heart, Lung, and Blood Institute · P01
Contact PI · $24.4M · Children's Hosp of Philadelphia
2000–2017
Pediatric Hematology Research Training Program
National Heart, Lung, and Blood Institute · T32
Contact PI · $3M · Children's Hosp of Philadelphia
1976–2017
Immune Responses to AAV-Mediated FIX Gene Transfer
National Heart, Lung, and Blood Institute · P01
Project lead · $3.5M · Wistar Institute
2005–2015
Pathway to Accelerate Clinical Development in Gene Transfer: cGMP Vector Core
National Center for Research Resources · G20
Contact PI · $2M · Children's Hosp of Philadelphia
2010–2014