
Michio Hirano
Chief, Division of Neuromuscular Medicine · New York Presbyterian Hospital
Credentials: · · ·
History
PresentDivision of Neuromuscular Medicine · New York Presbyterian Hospital
Presentthe H. Houston Merritt Neuromuscular Research Center · New York Presbyterian Hospital
PresentPreclinical Models · New York Presbyterian Hospital
1990–1991
1982–1986- 1978–1982
Harvard College
Research
Review · Nature Reviews Disease Primers · 2016 · 1,282 citations
Primary LAMP-2 deficiency causes X-linked vacuolar cardiomyopathy and myopathy (Danon disease)
Nature · 2000 · Last of 19 authors · 727 citations
Thymidine phosphorylase gene mutations in MNGIE, a human mitochondrial disorder
Science · 1999 · Last of 3 authors · 697 citations

43 papers · 8 as a resident

26 papers · 8 as a resident

24 papers

21 papers
- AK
14 papers

14 papers · 9 as a fellow

14 papers
- AH
13 papers
Grants
- 2011–2026
The North American Mitochondrial Disease Consortium (NAMDC)
National Institute of Neurological Disorders and Stroke · U54
Contact PI · $17.5M · Columbia University Health Sciences
- 2013–2023
Brief Research In Aging and Interdisciplinary Neurosciences (BRAIN)
National Institute on Aging · T35
PI · $1.1M · Columbia University Health Sciences
- 2018–2021
National Cancer Institute · R21
Contact PI · $377.6K · Columbia University Health Sciences
- 2014–2020
Mitochondrial Encephalomyopathies: Approaches to Treatment
National Institute of Child Health and Human Development · P01
PI · $7.8M · Columbia University Health Sciences
Clinical trials
- 2023–2026
Principal investigator · Recruiting · Phase 1
Michio Hirano, MD
- 2020–2026
- 2017–2026
Treatment of TK2 Deficiency With Thymidine and Deoxycytidine
Principal investigator · Active not recruiting · Phase 1, Phase 2
Columbia University
- 2015–2023
MNGIE Allogeneic Hematopoietic Stem Cell Transplant Safety Study
Principal investigator · Withdrawn · Phase 1
Michio Hirano, MD



