Nadia Kabbej

Disease correction in mucopolysaccharidosis type IIIB mice by intraparenchymal or cisternal delivery of a capsid modified AAV8 codon-optimized NAGLU vector

Human Molecular Genetics · 2023 · 8 citations

Femoral Structure and Biomechanical Characteristics in Sanfilippo Syndrome Type-B Mice

International Journal of Molecular Sciences · 2023 · 2 citations