Omar Khwaja

Pathogenesis of cerebral white matter injury of prematurity

Review · Archives of disease in childhood. Fetal and neonatal edition · 2008 · First of 2 authors · 497 citations

Discovery of Risdiplam, a Selective Survival of Motor Neuron-2 ( SMN2) Gene Splicing Modifier for the Treatment of Spinal Muscular Atrophy (SMA)

Journal of Medicinal Chemistry · 2018 · 418 citations