Ronald G. Crystal

Gene Therapy for Alpha 1-Antitrypsin Deficiency

National Heart, Lung, and Blood Institute · R33

Contact PI · $5M · Weill Medical Coll of Cornell Univ

Gene Therapy for APOE4 Homozygous Alzheimer's Disease

National Institute on Aging · UG3

Contact PI · $3.3M · Weill Medical Coll of Cornell Univ

Phase IA/IB Study of AAVrh.10hFXN Therapy to Treat the Cardiomyopathy of Friedreich's Ataxia

National Heart, Lung, and Blood Institute · R33

Contact PI · $5.9M · Weill Medical Coll of Cornell Univ

Gene Therapy to Treat Ethanol-Induced Osteoporosis Associated with Aldehyde Dehydrogenase 2 Deficiency in Post-Menopausal East Asian Women

National Institute on Alcohol Abuse and Alcoholism · R42

Contact PI · $2M · Enyx Therapeutics, Llc

Gene Therapy for Alpha 1- Antitrypsin Deficiency

Principal investigator · Recruiting · Phase 1

Weill Medical College of Cornell University

Phase IA and IB Study of AAVrh.10hFXN Gene Therapy for the Cardiomyopathy of Friedreich's Ataxia

Principal investigator · Recruiting · Phase 1

Weill Medical College of Cornell University

Administration of AdVEGF-All6A+ to Myocardium of Individuals With Diffuse CAD Via Minimally Invasive Surgery

Principal investigator · Withdrawn · Phase 1, Phase 2

Weill Medical College of Cornell University

Safety Study of a Disrupted Adenovirus (Ad) Serotype Cocaine Vaccine for Cocaine-dependent Individuals

Principal investigator · Recruiting · Phase 1

Weill Medical College of Cornell University