
Tippi MacKenzie
Director, Eli and Edythe Broad Center of Regeneration Medicine and Stem Cell Research at UCSF · University of California (San Francisco) School of Medicine
Credentials: · · ·
History
- Present
Eli and Edythe Broad Center of Regeneration Medicine and Stem Cell Research at UCSF · University of California (San Francisco) School of Medicine
- Present
Center for Maternal-Fetal Precision Medicine · University of California (San Francisco) School of Medicine
- Present
The Eli and Edythe Broader Center of Regeneration Medicine and Stem Cell Research · Stanford Health Care
- 2000–2002

Research
Nature Medicine · 2000 · 920 citations
Memory regulatory T cells reside in human skin
Journal of Clinical Investigation · 2014 · 292 citations
Large Differences in Small RNA Composition Between Human Biofluids
Cell Reports · 2018 · 191 citations

15 papers

15 papers · 13 as a fellow

13 papers · 11 as a resident

10 papers

9 papers
- MS
9 papers · 8 as a fellow

9 papers
- CJ
8 papers · 6 as a resident
Grants
- 2022–2030
Developing Genome Editing Strategies to Treat Alpha Thalassemia
National Heart, Lung, and Blood Institute · R01
Contact PI · $3.6M · University of California, San Francisco
- 2026–2029
Prenatal AAV9 Gene Replacement Therapy for Patients with Severe Infantile GM1 Gangliosidosis
National Institute of Neurological Disorders and Stroke · U01
Contact PI · $649.6K · University of California, San Francisco
- 2022–2027
Phase 1 Study of In Utero Enzyme Replacement Therapy for the Treatment of Lysosomal Storage Diseases
National Institute of Child Health and Human Development · R01
Contact PI · $3.3M · University of California, San Francisco
- 2019–2025
Autoimmune Regulator Gene (Aire)-Mediated Tolerance to Pregnancy-Associated Self-Antigens
National Institute of Allergy and Infectious Diseases · R01
Contact PI · $3.9M · University of California, San Francisco
Clinical trials
- 2028–2033
Prenatal Transplantation for Fetuses With Fanconi Anemia
Principal investigator · Not yet recruiting · Phase 1, Phase 2
Agnieszka Czechowicz
- 2026–2050
UCSF Center for Genome Surgery Biobank and Registry
Principal investigator · Recruiting
University of California, San Francisco
- 2022–2050
Registry of Patients Diagnosed With Lysosomal Storage Diseases
Principal investigator · Recruiting
University of California, San Francisco
- 2021–2032
PEARL (PrEnAtal Enzyme Replacement Therapy for Lysosomal Storage Disorders)
Principal investigator · Recruiting · Phase 1
University of California, San Francisco



