Fellowship · Iowa City, IA
Sponsored by University of Iowa Health Care Medical Center
Safety and efficacy of givinostat in boys with Duchenne muscular dystrophy (EPIDYS): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial.
The Lancet. Neurology · 2024 · 113 citations · Katherine Mathews
Safety and Efficacy of Omaveloxolone in Friedreich Ataxia (MOXIe Study).
Annals of neurology · 2021 · 248 citations · Katherine Mathews
Efficacy of Omaveloxolone in Friedreich's Ataxia: Delayed-Start Analysis of the MOXIe Extension.
Movement disorders : official journal of the Movement Disorder Society · 2023 · 95 citations · Katherine Mathews
Safety and efficacy of gene replacement therapy for X-linked myotubular myopathy (ASPIRO): a multinational, open-label, dose-escalation trial.
The Lancet. Neurology · 2023 · 106 citations · Dimah Saade
PIEZO2 in somatosensory neurons controls gastrointestinal transit.
Cell · 2023 · 115 citations · Dimah Saade
Phase 2 Trial of Rituximab in Acetylcholine Receptor Antibody-Positive Generalized Myasthenia Gravis: The BeatMG Study.
Neurology · 2022 · 99 citations · Michael Shy
Long-term survival of participants in the CENTAUR trial of sodium phenylbutyrate-taurursodiol in amyotrophic lateral sclerosis.
Muscle & nerve · 2021 · 141 citations · Andrea Swenson
Childhood amyotrophic lateral sclerosis caused by excess sphingolipid synthesis.
Nature medicine · 2021 · 135 citations · Dimah Saade