UCLA Medical Center Pediatric Hematology/Oncology

Topics

• Virus-based gene therapy research 163
• Hematopoietic Stem Cell Transplantation 70
• Childhood Cancer Survivors' Quality of Life 63
• Immunodeficiency and Autoimmune Disorders 60
• Sarcoma Diagnosis and Treatment 58
• CAR-T cell therapy research 49
• CRISPR and Genetic Engineering 35
• Glioma Diagnosis and Treatment 33
• Neuroblastoma Research and Treatments 31
• Acute Lymphoblastic Leukemia research 28
• Hemoglobinopathies and Related Disorders 28
• Acute Myeloid Leukemia Research 25

Most cited

1. GD2-CAR T cell therapy for H3K27M-mutated diffuse midline gliomas.

   Nature · 2022 · 697 citations · Aaron Mochizuki

2. Generation of allogeneic CAR-NKT cells from hematopoietic stem and progenitor cells using a clinically guided culture method.

   Nature biotechnology · 2025 · 88 citations · Donald Kohn

3. Nirogacestat, a γ-Secretase Inhibitor for Desmoid Tumors.

   The New England journal of medicine · 2023 · 219 citations · Noah Federman

4. Adolescent and Young Adult (AYA) Oncology, Version 2.2024, NCCN Clinical Practice Guidelines in Oncology.

   Journal of the National Comprehensive Cancer Network : JNCCN · 2023 · 146 citations · Noah Federman

5. Measuring the effect of newborn screening on survival after haematopoietic cell transplantation for severe combined immunodeficiency: a 36-year longitudinal study from the Primary Immune Deficiency Treatment Consortium.

   Lancet (London, England) · 2023 · 108 citations · Theodore Moore, Donald Kohn

6. Successes and challenges in clinical gene therapy.

   Gene therapy · 2023 · 127 citations ·