AP
Amy Pasternak
Specialist
Credentials: ·
History
Research
Patient-Customized Oligonucleotide Therapy for a Rare Genetic Disease
Case report · New England Journal of Medicine · 2019 · 642 citations
Revised upper limb module for spinal muscular atrophy: Development of a new module
Muscle & Nerve · 2017 · 255 citations
Patterns of disease progression in type 2 and 3 SMA: Implications for clinical trials
Neuromuscular Disorders · 2016 · 149 citations
- BD
43 papers
38 papers
34 papers
28 papers
27 papers
- SY
18 papers
10 papers
- GT
8 papers
Clinical trials
- 2024–2028
Site PI · Recruiting
Columbia University