AD
April DeStefano
Neurology Residency · University of Vermont Medical Center
Credentials: ·
History
- 2023–Present
- 2019–2023
- 2015–2019
Douglas College at Rutgers - BS
Research
A single amino acid variant in the variable region I of AAV capsid confers liver detargeting
PLoS Pathogens · 2025 · 3 citations
A compact base editor rescues AATD-associated liver and lung disease in mouse models
Molecular Therapy · 2025 · 2 citations
- TF
4 papers
- JY
2 papers