Dwight Koeberl

Stable Therapy in Pompe Disease Through Genome Editing

National Institute of Arthritis and Musculoskeletal and Skin Diseases · R01

Contact PI · $3.3M · Duke University

Genome Editing for the Correction of Pompe Disease

National Institute of Arthritis and Musculoskeletal and Skin Diseases · R21

Contact PI · $373.2K · Duke University

Investigating Autophagy in GSD-Ia

National Institute of Diabetes and Digestive and Kidney Diseases · R56

Contact PI · $159.2K · Duke University

Investigating Autophagy in GSD-Ia

National Institute of Diabetes and Digestive and Kidney Diseases · R01

Contact PI · $1.3M · Duke University

Phase II Clinical Trial of Clenbuterol in Adult Patients With Pompe Disease

Principal investigator · Withdrawn · Phase 2

Duke University

Pompe Gene Therapy- Screening for Eligibility

Principal investigator · Completed

Duke University

Safety and Efficacy of Clenbuterol in Individuals With Late-onset Pompe Disease and Receiving Enzyme Replacement Therapy

Principal investigator · Completed · Phase 1, Phase 2

Dwight Koeberl, M.D., Ph.D.

Safety and Efficacy of Albuterol in Individuals With Late-onset Pompe Disease

Principal investigator · Completed · Phase 1, Phase 2

Duke University