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ES

Edward Smith

Pediatrics

Credentials: · · · ·

History

Pediatrics
Duke University Hospital
2004–2007
Child Neurology
Duke University Hospital
2002–2005
University of Mississippi School of Medicine
1998–2002

Research

Onasemnogene abeparvovec gene therapy for symptomatic infantile-onset spinal muscular atrophy in patients with two copies of SMN2 (STR1VE): an open-label, single-arm, multicentre,…
The Lancet Neurology · 2021 · 399 citations
Safety, Tolerability, and Efficacy of Viltolarsen in Boys With Duchenne Muscular Dystrophy Amenable to Exon 53 Skipping: A Phase 2 Randomized Clinical Trial
JAMA Neurology · 2020 · 229 citations
Efficacy and Safety of Vamorolone vs Placebo and Prednisone Among Boys With Duchenne Muscular Dystrophy: A Randomized Clinical Trial
JAMA Neurology · 2022 · 114 citations

Craig McDonald
16 papers
PC
Paula Clemens
14 papers
Nancy Kuntz
11 papers
Anne Connolly
10 papers
AH
Amy Harper
9 papers
Richard Finkel
9 papers
DC
Diana Castro
8 papers
Vandana Shashi
8 papers
Perry Shieh
7 papers
Russell Butterfield
7 papers
Aravindhan Veerapandiyan
6 papers · 2 as a fellow
Dwight Koeberl
6 papers