Jeremy Rupon

Gene Therapy with Fidanacogene Elaparvovec in Adults with Hemophilia B

New England Journal of Medicine · 2024 · 85 citations

Methyl binding domain protein 2 mediates gamma-globin gene silencing in adult human betaYAC transgenic mice

Proceedings of the National Academy of Sciences of the United States of America · 2006 · First of 5 authors · 65 citations