
Richard Shell
Pediatrics / Pediatric Pulmonology · Pediatric Academic Association, Inc.
Credentials: · ·
History
Research
Single-Dose Gene-Replacement Therapy for Spinal Muscular Atrophy
New England Journal of Medicine · 2017 · 1,837 citations
JAMA Neurology · 2020 · 331 citations
Natural history of infantile-onset spinal muscular atrophy
Annals of Neurology · 2017 · 331 citations

9 papers
- JK
8 papers

7 papers

7 papers

6 papers

6 papers
- SA
6 papers
- BD
5 papers




