SA
Samiah Al-Zaidy
Psychiatry & Neurology / Neurology with Special Qualifications in Child Neurology
Credentials: · ·
Research
Single-Dose Gene-Replacement Therapy for Spinal Muscular Atrophy
New England Journal of Medicine · 2017 · 1,837 citations
Current Clinical Applications of In Vivo Gene Therapy with AAVs
Review · Molecular Therapy · 2021 · 578 citations
JAMA Neurology · 2020 · 331 citations

18 papers

Kelly Lehman
7 papers

6 papers
- ZS
6 papers
- JK
5 papers

4 papers
- DS
4 papers

4 papers


