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SN

Sukumar Nagendran

Internal Medicine

Credentials: · ·

History

Internal Medicine

Research

Single-Dose Gene-Replacement Therapy for Spinal Muscular Atrophy
New England Journal of Medicine · 2017 · 1,837 citations
Impact of Age and Motor Function in a Phase 1/2A Study of Infants With SMA Type 1 Receiving Single-Dose Gene Replacement Therapy
Pediatric Neurology · 2019 · 146 citations
AVXS-101 (Onasemnogene Abeparvovec) for SMA1: Comparative Study with a Prospective Natural History Cohort
Journal of Neuromuscular Diseases · 2019 · 138 citations

David Arnold
3 papers
DS
Douglas Sproule
3 papers
Jerry Mendell
3 papers
JK
John Kissel
3 papers
JR
Julio Rosenstock
3 papers
Richard Shell
3 papers
SA
Samiah Al-Zaidy
3 papers
YH
Yehuda Handelsman
3 papers
DF
Douglas Feltner
2 papers
Ronald Goldberg
2 papers
Vivian Fonseca
2 papers
William Garvey
2 papers