Barry Byrne

Procession to IND of a Capsid Mutated AAV8 Codon Optimized NAGLU Vector for Treatment of Sanfilippo Syndrome Type B

National Institute of Neurological Disorders and Stroke · UH3

PI · $470.2K · University of Florida

Control of Breathing and Pompe Disease

National Institute of Child Health and Human Development · R01

Contact PI · $4.9M · University of Florida

Procession to IND of a Capsid Mutated AAV8 Codon Optimized NAGLU Vector for Treatment of Sanfilippo Syndrome Type B (Supplement)

National Institute of Neurological Disorders and Stroke · UG3

PI · $1.7M · University of Florida

Phase II Study of AAV9-GAA Gene Transfer in Pompe Disease

National Heart, Lung, and Blood Institute · U01

Contact PI · $1.6M · University of Florida

A Pilot Study of Zavesca® in Patients With Pompe Disease and Infusion Associated Reaction

Principal investigator · Terminated · Phase 1

University of Florida

A Pilot Study of Pyridostigmine in Pompe Disease

Principal investigator · Terminated · Early phase 1

University of Florida

Assessment of Cardiopulmonary Function in Duchenne Muscular Dystrophy

Principal investigator · Completed

University of Florida

Safety Study of Recombinant Adeno-Associated Virus Acid Alpha-Glucosidase to Treat Pompe Disease

Principal investigator · Completed · Phase 1, Phase 2

University of Florida