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Carmen Astudillo

To Associate Professor · University of Florida College of Medicine

Credentials: · · · ·

History

University of Florida College of Medicine
Present

Pediatric Pulmonology
Boston Childrens Hospital
2015–2018
Pediatrics
Cincinnati Children's Hospital Medical Center
2012–2015
Doctor of Medicine
2006–2010

Research

AAV gene therapy for Duchenne muscular dystrophy: the EMBARK phase 3 randomized trial
Nature Medicine · 2025 · 143 citations
Thrombotic microangiopathy following systemic AAV administration is dependent on anti-capsid antibodies
Journal of Clinical Investigation · 2024 · 115 citations
Current clinical applications of AAV-mediated gene therapy
Review · Molecular Therapy · 2025 · 87 citations

Barry Byrne
14 papers
DC
Diana Castro
4 papers
Aravindhan Veerapandiyan
3 papers
Caroline Okorie
3 papers
Craig McDonald
3 papers
Craig Zaidman
3 papers
CP
Crystal Proud
3 papers
FD
Fei Dy
3 papers
Jane Gross
3 papers
John Brandsema
3 papers
Andres Gomez
2 papers · 2 as a resident
BD
Basil Darras
2 papers

Clinical trials

A Gene Transfer Therapy Study to Evaluate the Safety of and Expression From Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD) - Non-Ambulatory Cohort
Site PI · Recruiting · Phase 1
Sarepta Therapeutics, Inc.
2020–2028